Disc Medicine is laying off a fifth of its workforce as the biotech reels from the FDA’s rejection of its rare blood disease candidate. | Disc Medicine is laying off a fifth of its workforce as the ...

Odisha's health department has introduced two advanced medicines for haemophilia and Von Willebrand disease patients, marking a first for the state. These extended half-life Factor VIII and Von ...

Scientists have uncovered the precise molecular trigger behind a rare blood-clotting disorder linked to certain COVID-19 vaccines.

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

At 11 years old, Mykela Shields has experienced more hospital stays, tests and procedures than most people will in their lifetime. Her memories consist of the pinch of a blood draw, the ...

“This partnership marks a major milestone in our mission to transform how rare disease therapies reach patients in Europe,” said Adam Plich, Founder and CEO of Avanzanite. “We provide biotech partners ...

WASHINGTON — The Food and Drug Administration has approved the first drug treatment for pediatric patients 12 and older with a rare blood disorder. The treatment for acquired thrombotic ...

A 19-year-old Canadian man becomes the first human cured through prime gene editing after doctors corrected a rare genetic ...

Juan Uribe's 15-year-old son Max needs a perfect stem cell donor match. His story went viral on social media, but the search ...

America's 250: Red, White & You: Eliza Newton, a 14-year-old BMX champion, triumphs over aplastic anemia with a life-saving bone marrow transplant.

Gus’ former junior rugby league club the Walkerston Wanderers started a group to donate blood and plasma joining a ...